Gene Therapy MCQs with Answers

Which delivery method involves extracting cells, modifying them in vitro, and reinfusing them into the patient?

What is the main purpose of gene therapy?

Which term describes a stable integration of introduced genes into the host cell's genome?

Which term describes the technique of introducing DNA into cells using electric shock?

Which enzyme is commonly used in CRISPR gene editing to cut DNA at specific sequences?

Which of these is a potential ethical concern in gene therapy?

What is the term for gene therapy that targets cancer cells specifically?

What is the primary reason for using CRISPR/Cas9 in gene therapy?

Which of these is a potential challenge in delivering gene therapy to the brain?

Which of these is a potential safety concern in using CRISPR/Cas9 for gene therapy?

What is the primary advantage of using lentiviral vectors in gene therapy?

Which term describes the process of introducing genes into stem cells to treat genetic disorders?

Which of these is a potential side effect of gene therapy using viral vectors?

Which of the following is an example of a monogenic disorder that could be treated with gene therapy?

What is the term for a segment of DNA that is capable of moving and replicating within the genome?

Which regulatory agency oversees the approval of gene therapy products in the United States?

What is the term for gene therapy aimed at modifying germ cells (sperm or egg cells)?

What is the most common route of administration for gene therapies targeting the liver?

In which phase of clinical trials is gene therapy typically tested for safety and efficacy?

Which term describes the transfer of genetic material from one organism to another?

What is the term for a vector that can replicate independently of the host cell's genome?

Which type of viral vector is derived from adenovirus and commonly used in gene therapy?

What is the term for a gene that can cause cancer when mutated or overexpressed?

Which type of gene therapy aims to correct genetic mutations in mitochondrial DNA?

Which of these is a potential limitation of CRISPR/Cas9 technology in gene therapy?

Which of the following is NOT a potential application of gene therapy?

Which of the following is a potential advantage of using non-viral vectors in gene therapy?

Which of the following is a non-viral vector used in gene therapy?

What is the term for the process of introducing new genetic material into cells to correct a genetic defect?

What is the primary challenge of using viral vectors in gene therapy?

Which vector is commonly used in gene therapy to deliver genes into target cells?

In gene therapy, what does the acronym "CRISPR" stand for?

Which gene therapy approach involves inserting a new gene into a random location in the genome?

Which type of gene therapy involves correcting mutations in the DNA of mitochondria?

Which regulatory challenge is specific to gene therapy compared to traditional drugs?

What is the term for a regulatory sequence that controls the timing and level of gene expression?

Which delivery method involves directly injecting the therapeutic vector into the affected tissue?

What is the term for gene therapy aimed at modifying somatic cells?

Which type of gene therapy aims to inhibit the expression of a particular gene?

Which term describes the delivery of genetic material using ultrasound?